Gene Therapy Trial Succeeds In Boosting Protective Protein In Patients With Hereditary Lung Disease, University of Massachusetts Medical School Study

University of Massachusetts -- WORCESTER, Mass. – Researchers at the University of Massachusetts Medical School and the University of Florida in Gainesville have safely given new, functional genes to patients with a hereditary defect that can lead to fatal lung and liver diseases, according to clinical trial findings slated to appear this week in the online early edition of the Proceedings of the National Academy of Science.