Gene therapy

Drug Development

First ever CRISPR gene therapy approval: What happens next?

CRISPR gene-editing has had its first ever approval in the UK. Will the FDA follow suit? What can patients expect the price tag to be?

November 21, 2023

·

1 min read

·

PRESS RELEASES

Press Releases

Clinical Milestones, Vector Innovation Key to Gene Therapy, GenoTher Biocluster’s First International Summit, Atamyo Therapeutics’ Progress for LGMDs Highlight Genethon’s Most Recent Newsletter

June 19, 2025

·

2 min read

Press Releases

64x Bio Launches AAV Apex Suite to Power the Next Generation of Gene Therapy Manufacturing

June 16, 2025

·

2 min read

Press Releases

Fractyl Health to Present New Preclinical Data from its Rejuva® Smart GLP-1™ Pancreatic Gene Therapy Platform at the American Diabetes Association’s 85th Scientific Sessions

June 16, 2025

·

2 min read

Press Releases

Sarepta Provides Safety Update for ELEVIDYS and Initiates Steps to Strengthen Safety in Non-Ambulatory Individuals with Duchenne

June 16, 2025

·

12 min read

Press Releases

Adolore BioTherapeutics Announces Publication Demonstrating Biosafety and Efficacy of Kv7 Activating rdHSV-CA8* Analgesic Gene Therapy for Chronic Pain via the Intra-Articular Route in Mice

June 16, 2025

·

6 min read

Press Releases

Mission Bio Unveils Industry-First Single-Cell Genotype and Targeted Gene Expression Solution Aimed at Derisking Cancer Drug Clinical Development

June 6, 2025

·

5 min read

Press Releases

MarkHerz Signs MOU with TUM Hospital for Joint Development of Cardiovascular and Diabetes-Targeted AAV Gene Therapies

June 3, 2025

·

4 min read

Press Releases

Beghou Consulting Adds New Partners to Strengthen Market Access, Cell & Gene Therapy, and Technology Capabilities

May 29, 2025

·

3 min read

Press Releases

Capsida Receives FDA Fast Track Designation for Its Potential First-in-Class IV-Administered Gene Therapy for STXBP1 Developmental and Epileptic Encephalopathy

May 29, 2025

·

3 min read

Press Releases

Genprex to Present Trial Design of Acclaim-3 Clinical Trial Evaluating Reqorsa® Gene Therapy in Small Cell Lung Cancer at 2025 ASCO Annual Meeting

May 29, 2025

·

9 min read

Press Releases

uniQure Presents Clinical Case Study of First Patient Dosed with AMT-260 in Refractory Mesial Temporal Lobe Epilepsy (MTLE)

May 29, 2025

·

6 min read

Press Releases

Medable Introduces Long-Term Follow-Up Model for Cell & Gene Therapy (CGT) Trials to Reduce Costs and Improve Patient Access

May 28, 2025

·

3 min read

Press Releases

Genflow Biosciences and CER Sign Master Service Agreement to Strengthen Long-Term R&D Collaboration

May 28, 2025

·

2 min read

Press Releases

Ocugen Announces Rare Pediatric Disease Designation Granted for OCU410ST—Modifier Gene Therapy for the Treatment of Stargardt Disease

May 28, 2025

·

5 min read

Press Releases

Spur Therapeutics Publishes Preclinical Proof-of-Concept Data for FLT201, its Clinical-Stage Gene Therapy Candidate in Gaucher Disease

May 28, 2025

·

3 min read

Press Releases

Alfred E. Mann Charities Gives $12 Million for Cell and Gene Therapy Research at Children’s Hospital Los Angeles

May 21, 2025

·

4 min read

Press Releases

Coave Therapeutics Establishes New Scientific Advisory Board to Accelerate Innovation in Genetic Medicines for Eye and CNS Diseases

May 21, 2025

·

4 min read

Press Releases

Genethon Presents Two Year Consolidated Results of Its Gene Therapy Trial for Duchenne Muscular Dystrophy: Maintenance of Motor Functions and Significant, Sustained Reduction in CPK Levels in Patients Treated at the Effective Dose at ASGCT 2025

May 19, 2025

·

4 min read

Press Releases

LIfT BioSciences presents latest data on its first-in-class Immunomodulatory Alpha Neutrophils at International Society for Cell and Gene Therapy

May 19, 2025

·

3 min read

Press Releases

Intellia Announces Positive Two-Year Follow-Up Data from Ongoing Phase 1 Study of Nexiguran Ziclumeran (nex-z), in Patients with Hereditary Transthyretin (ATTR) Amyloidosis with Polyneuropathy at Peripheral Nerve Society Annual Meeting

May 19, 2025

·

10 min read