Gene therapy

Deals

Grab an umbrella, it’s raining ⁠IPOs⁠!

This week, Lori, Greg and Tyler discuss the first ⁠surge of IPO activity⁠ this year plus gene therapy pricing,

January 23, 2024

1 min read

Lori Ellis

Drug Development

First ever CRISPR gene therapy approval: What happens next?

CRISPR gene-editing has had its first ever approval in the UK. Will the FDA follow suit? What can patients expect the price tag to be?

November 21, 2023

1 min read

Greg Slabodkin

PRESS RELEASES

Press Releases

Modalis Announces Publication in Human Gene Therapy of Study Demonstrating Efficient LAMA1 Gene Activation for the Treatment of LAMA2-CMD

December 25, 2025

3 min read

Press Releases

GenSight Biologics Announces Regulatory Authorization for Early Access Treatment with GS010/LUMEVOQ® in Israel

December 23, 2025

5 min read

Press Releases

GenSight Biologics Announces the Granting of Compassionate Use Authorization (CUA/AAC) for GS010/LUMEVOQ® in France

December 22, 2025

2 min read

Press Releases

Minaris and Cell and Gene Therapy Catapult Announce Collaboration to Advance Delivery Methods for Cell and Gene Therapies

December 19, 2025

4 min read

Press Releases

Beacon Therapeutics Treats First Patient in LANDSCAPE Trial of laru-zova in Patients with X-linked Retinitis Pigmentosa (XLRP)

December 17, 2025

4 min read

Press Releases

RoslinCT and Ayrmid Ltd. Announce Expansion of Strategic Partnership to Manufacture Omisirge® (omidubicel-onlv) for Second FDA-Approved Indication in Severe Aplastic Anemia (SAA)

December 16, 2025

3 min read

Press Releases

Genflow Completes Dosing Phase of Canine Gene Therapy Trial

December 16, 2025

6 min read

Press Releases

Cure Rare Disease Awarded $7.4 Million CIRM Grant to Advance Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2i/R9

December 16, 2025

3 min read

Press Releases

Thermo Fisher Scientific Expands Gibco™ Bacto™ Portfolio with Next-Generation, Chemically Defined Media to Boost E. coli Biomanufacturing Productivity

December 16, 2025

4 min read

Press Releases

Fondazione Telethon and Orphan Therapeutics Accelerator Sign Memorandum of Understanding to Pioneer Non-Profit Commercial Access Model for Ultra-Rare Disease Gene Therapy in the US

December 16, 2025

6 min read

Press Releases

Tenaya Therapeutics Announces Rapid Resolution and Lifting of Clinical Hold for MyPEAK-1™ Phase 1b/2a Clinical Trial of TN-201 Gene Therapy

December 12, 2025

7 min read

Press Releases

Tenaya Therapeutics Reports Positive Interim Data from Cohort 1 of RIDGE™-1 Phase 1b/2 Clinical Trial of TN-401 Gene Therapy for Adults with PKP2-associated ARVC

December 12, 2025

11 min read

Press Releases

Charles River Extends Commitment to Advanced Therapy Developers with Second Incubator Program Cohort

December 12, 2025

7 min read

Press Releases

EpilepsyGTx Raises $33 Million Series A to Develop Single Dose Gene Therapy for Focal Refractory Epilepsy

December 11, 2025

3 min read

Press Releases

Fondazione Telethon Announces FDA approval of Waskyra™ (etuvetidigene autotemcel), a Gene Therapy for the Treatment of Wiskott-Aldrich Syndrome

December 10, 2025

5 min read

Press Releases

Aradigm Launches First-of-Its-Kind Platform to Provide Sustainable Access to Life-Saving Cell and Gene Therapies

December 10, 2025

5 min read

Press Releases

Genetix Presents Recent Patient Experience Data from U.S. Commercial Gene Therapy Implementation at the 67th American Society of Hematology (ASH) Annual Meeting

December 9, 2025

15 min read

Press Releases

Andelyn Biosciences Announces Partnership with Jaguar Gene Therapy to Provide Late-Stage PPQ Manufacturing

December 8, 2025

5 min read

Press Releases

Solid Biosciences to Showcase Proprietary Next-Generation Capsid AAV-SLB101 and Cardiac Gene Therapy Pipeline at the 22nd Global CardioVascular Clinical Trialists (CVCT) Forum

December 8, 2025

6 min read

Press Releases

Abeona Therapeutics® Announces First Patient Treatment with ZEVASKYN® Gene Therapy

December 8, 2025

6 min read