Trial Therapy May Fight Genetic Disorders

A combination of gene therapy and stem cell therapy may offer a new way to correct inherited diseases, says a University of Florida study. In research with mice with damaged livers, the scientists removed liver cells called progenitors that have the ability of stem cells to rebuild damaged organs. These progenitor cells were equipped with a healthy human gene and then placed back in the mice. The progenitor cells than began to rebuild the liver with cells that expressed the healthy human gene.

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