Orchard Therapeutics, a global gene therapy leader, announced a range of interim clinical outcomes, in addition to the previously reported neurological and skeletal results, from the company’s ongoing proof-of-concept study of OTL-203, a hematopoietic stem cell gene therapy in development for the treatment of the Hurler subtype of mucopolysaccharidosis type I.
October 26, 2023
· 9 min read