Introduction to RNA-Targeting Therapeutics

ABOUT THE EVENT

Date: Friday, January 23, 2026 8–9am PST
Event Location: Virtual

📅 January 23rd, 8:00 AM PSTThis opening session provides a practical foundation for understanding how mutation-specific RNA therapies are designed, engineered, and deployed in clinical settings. Topics include precision targeting, turning genes up or down, correcting splicing errors, minimizing off-target effects, and real-world clinical examples from diseases such as SMA, DMD, and ALS.

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Tuesday, February 24, 2026 12–1pm EST
 · 
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