Shionogi & Co., Ltd. announced the U.S. Food and Drug Administration (FDA) has granted Tetra Therapeutics Inc. (hereafter “Tetra”), a Shionogi Group Company, Rare Pediatric Disease Designation for zatolmilast (BPN14770), an investigational treatment being studied for Fragile X syndrome (FXS), a leading cause of inherited intellectual disability and autism.
September 27, 2023
· 6 min read