Voyager Therapeutics, Inc., a gene therapy company developing life-changing treatments and next-generation platform technologies, introduced new programs in Huntington’s disease, a monogenic form of ALS, spinal muscular atrophy, and diseases linked to GBA1 mutations, all powered by its proprietary AAV capsids that have demonstrated superior transgene expression in the brain compared to AAV9 delivery in non-human primates.
August 9, 2021
· 14 min read