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Ashley P. Taylor

Pictured: a young boy with an oxygen mask/iStock,
Drug Development
ReCode, Vertex and 4DMT Seek to Help Untreated Cystic Fibrosis Patients
Drugs that act on the CFTR protein only work in patients who produce the protein in the first place. That leaves 6% of patients hanging.
June 1, 2023
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7 min read
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Ashley P. Taylor
Sickle cell anemia, 3D illustration showing blood vessel with normal and deformed crescent
Drug Development
Bluebird Submits BLA for Sickle-Cell Disease Gene Therapy
The regulatory filing puts the company alongside Vertex and CRISPR, which also await FDA approval for their SCD gene therapy.
April 25, 2023
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4 min read
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Ashley P. Taylor