Q-State Biosciences (“Q-State”), today announced the publication of new research describing the successful design, screening and characterization of splice modulating antisense oligonucleotides (ASOs) as a potential therapeutic approach for SPG49/HSAN9 (spastic paraplegia 49, more recently classified as hereditary sensory and autonomic neuropathy type IX), an ultra-rare neurodevelopmental and neurodegenerative disorder.
July 7, 2022
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