Orphan Technologies, a company dedicated to helping patients control their homocysteine levels, today announced that OT-58 for the treatment of cystathionine beta synthase deficiency homocystinuria has been designated a rare pediatric disease (RPD) by the US Food and Drug Administration (FDA). Under the RPD program, if a new drug application for OT-58 is approved,
March 26, 2020
· 3 min read