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Executive Director, US Medical Lead, Growth Related Conditions

BioMarin Pharmaceutical Inc.
Working from Home
Start date
Apr 19, 2024

Job Details

This position is embedded in the US Medical Affairs organization and is responsible for medical leadership for BioMarin’s growth-related conditions medicines and programs. This responsibility includes leadership and direction across US medical team to ensure strategic alignment and integration at the global level of regionally driven priorities. This individual will interface externally with healthcare professionals, clinical investigators, regulatory agencies amongst others as well as with cross-functional internal BioMarin teams providing medical insights to drive scientific strategy within integrated brand plans and to inform clinical development and life cycle plans related to this therapeutic area. This individual will be the scientific reference point at the US level, representing the department and the company at key internal and external activities and events in relation to the therapeutic area.                                                                                                                                                                                           KEY RESPONSIBILITIES:  Medical Lead – US Medical
  • Lead US medical strategic planning, prioritization, and execution oversight of Growth Conditions medical activities. Assign and align functionally and cross-functionally on objectives, deliverables, roles & responsibilities
  • Partnering with cross-functional BioMarin teams (including marketing, market access, clinical development and others) in the development and execution of integrated VOXZOGO brand and launch strategies, robust LCM and pipeline development plans
  • Ensuring timely GMAF leadership team awareness and alignment on key program needs and opportunities and ensure representation of GMAF aligned position in internal and external forums and processes
  • Providing medical input into development, execution, and interpretation of clinical protocols.  This includes review of draft independent research protocols, reports, and manuscripts; oversight of clinical registries and other post-marketing commitment; support evaluation of safety issues in collaboration with Medical Monitors and other teams; review of study results in study reports
  • Develop high-performing US medical Growth related Conditions team of direct reports and matrix partners.
  • Direct interaction with investigators, KOLs and the research community to support company initiatives. Responsible for representing BioMarin at scientific, clinical, and business development meetings. Promote effective communication between internal and external groups regarding Medical Affairs initiatives
  • Responsible for partnering in the cross-functional development of key scientific and medical narrative for core data documents, publications, and communications, including identification of data gaps and proactive resolution
  • Drive strategic congress planning for Achondroplasia key congresses and align cross-functionally on objectives, key messages and plans at key US conferences
  • Ensure compliance with policies, SOPs, Code of Business Conduct and Corporate Social Responsibility, as well as relevant legislation and regulations
Personal Qualities      
  • Ability to work proactively and effectively, with exceptional creative problem-solving skills and self-motivation.
  • Ability to lead a cross-functional teams within a matrix type organizational structure
  • Ability and agility to develop and maintain scientific and clinical knowledge and expertise to a level required as subject matter expert in growth related consitions
  • Develop, retain and motivate direct reports (medical directors) and integration with matrix team with clear delineation of accountabilities
  • Ability to promote effective communication between internal and external groups. Collaborative and flexible in personal interactions at all levels of the company
  • Able to thrive in an ambiguous and demanding environment, with high capacity for effective relationship building and teamwork
  • Flexibility and adaptability. Sensitivity to a multicultural environment
  • Excellent written and oral communication skills. Able to convince, inspire and motivate people with a variety of backgrounds
  • Solid business acumen with high scientific inquisitiveness
  • Willingness to travel approx. 20-40% of the time, including internationally
  • Advanced Degree (M.D. / Ph.D. / PharmD) in Medicine and/or a medical sciences field
  • Very strong industry experience, especially in Medical Affairs (≥ 7 years)
  • Experience in pediatric endocrinology preferred
  • Understand US Healthcare compliance landscape. Knowledgeable of current GCP guidelines and compliance rules. Clinical trial and publication experience is desirable
  • Demonstrate excellent medical affairs skills and ideally have working knowledge in the therapy area
  • Experience in Skeletal Dysplasia highly desirable, either in pharmaceutical/clinical research or a clinical environment
  • Experience in rare diseases or genetic medicine highly desirable
Note: This description is not intended to be all-inclusive, or a limitation of the duties of the position. It is intended to describe the general nature of the job that may include other duties as assumed or assigned. We are an equal opportunity employer, and all qualified applicants will receive consideration for employment without regard to race, color, religion, gender, gender identity, sexual orientation, national origin, disability status, protected veteran status, or any other characteristic protected by law. 


BioMarin is a global biotechnology company dedicated to transforming lives through genetic discovery. In 1997, the company was founded to make a big difference in small patient populations, focusing on giving much-needed attention to the underserved communities of those with rare diseases. BioMarin sought to help patients whose voices could not always be heard and treat conditions that were not always in mainstream medical conversations. Throughout its history, BioMarin has worked tirelessly to make a difference by pursuing bold science. The company’s first approved therapy was inspired by a father who refused to accept there was no therapy for his son’s rare diagnosis. That relentless pursuit to change the course of his son’s future through the power of science is at the core of who BioMarin is today.

Through the company’s expertise in genetics and molecular biology, BioMarin has developed eight first or best-in-class targeted therapies that address the root cause of the conditions it seeks to treat, helping to better the lives of those struggling with rare genetic disease. The company’s purposeful and scientifically precise team of physicians and scientists has honed each treatment modality to seek transformative therapies.

Now, BioMarin seeks to make an even greater impact by applying the same science-driven, patient-forward approach that propelled the last 25 plus years of drug development to larger genetic disorders, as well as genetic subsets of more common conditions. Each drug candidate pursued is guided by a fundamental understanding of the genetics and underlying biology of the condition it will address. The company believes that applying its knowledge to make a transformative impact is not just a calling, but an obligation to those who will benefit most. The more innovative solutions developed, the more lives BioMarin can impact.

Company info
United States

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