Senior Director, Global Patient Access - SMA

Bannockburn, IL, US
Sep 10, 2020
Required Education
Masters Degree/MBA
Position Type
Full time


Ready to join a team committed to developing and commercializing gene therapies for patients and families devastated by rare neurological genetic diseases? Since 2013, Novartis Gene Therapies (formerly AveXis) has had one focus: bringing change to those devastated by genetic diseases.

The Novartis Gene Therapies culture embraces this mission. As a compassionate and dedicated team, we are enthusiastic about the science behind our work and finding answers to difficult questions. We are dedicated to communities affected by rare diseases, and these patients and families are the motivation for everything we do.

We have built a team with exceptional depth of experience, unified by a common vision; to develop gene therapies with the potential to positively impact the lives of the patients and families devastated by rare and life-threatening neurological genetic diseases. Though we are proud of what we have achieved to date, we remain relentlessly focused on making that vision a reality.

The Senior Director, Global Patient Access - SMA is a core member of the Global Patient Access leadership team. This role is responsible for developing and implementing integrated market access strategies to ensure the successful launch and growth of AVXS-101 globally. The focus of this role is on the company's lead program, AVXS-101 in SMA; over time, other product candidates and diseases may be under the scope of this role.



  • Ensuring global market access strategies are aligned with global program team; global commercial strategies; and corporate including positioning.
  • Serves as a primary point of contact for the patient access function for all cross-functional stakeholders related to market access globally.
  • Leads the development of global Value and Access integrated strategy and AVX101 to maximize product value and ensure optimal global patient access (including IT formulation and IV expansion)
  • Partners closely with HEOR, RWE, R&D, Medical Affairs, global and local commercial counterparts to ensure market access inputs are incorporated into clinical development, medical affairs and commercial strategies.
  • As a core member of the global program team (GPT) partner with key functions and regional leadership to drive implementation of global access strategy, refinement of AVXS-101 value proposition and core value messages, and ongoing global negotiation strategy.
  • Assesses and defines evidence needs across global priority markets and develop integrated evidence generation strategies and plans in collaboration with global patient access functions (HEOR, RWE, Pricing; Analytics).
  • Supports global launch readiness of AVXS-101 and implementation of market access, pricing, and reimbursement plan, in partnership with the global commercial team and regional commercial and market access leads.
  • Leads cross-functional team global health economics; real world evidence to ensure all initiatives (e.g., HEOR, Market Access, RWE Business Insights, Policy) are fully integrated, aligned and on-schedule to support the value of AVXS-101.
  • Develops SMA value story and shape plans to deliver against vision by conducting regular payer research as needed to refine value perception, landscape, evolving trends and value drivers.
  • Collaborates with cross-functional teams to incorporate access considerations into market assessment, product positioning, target product profiles and clinical development strategy
  • Works closely with regional leadership, to optimize support from patient groups, to shape a favorable policy environment for access, including newborn screening for SMA.
  • Supports global pricing operations (pricing strategy implementation, pricing approval process, etc.) and drive efficient pricing governance.
  • Supports value communication plan and execution in close collaboration with Public Relations, Investor Relations, Medical Affairs, Commercial, and other key stakeholders.
  • Instills, supports, is a role model of a culture of ethics and integrity.
  • Oversight and management of approved budgets.
  • Maintain industry awareness in scope of responsibilities regarding external landscape and trends.
  • Other related duties as assigned.




  • Bachelors' of science (or similar degree) with 10 years' experience as a market access leader that includes the launch and commercialization of innovative, first-in-class specialty pharmaceutical products across several regions internationally. An advanced degree (Masters, Doctorate, or similar degree) is preferred.
  • Successfully held a role of similar capacity at another company as well as having experience in emerging markets is preferred.
  • Ability to work across multiple functions, geographies and cultures and in a company with global functions in the U.S.
  • Prior experience in rare diseases, in high-value products, and in a small, rapidly growing company are preferred.
  • Strong written and verbal communication skills in English is required and proficiency in one of the major languages spoken in the region is preferred.
  • Demonstrated experience in the development and execution of market access plans for highly specialized products.
  • Successful first-hand ex-US experience in pricing, reimbursement and access for high-value products in rare diseases, including at least the EU5/UK, with experience in emerging markets preferred.
  • Experience in developing and executing risk-sharing agreements and in-country outcomes registries in partnership with HEOR and Medical Affairs.
  • A penchant for the science and economics of medicines and a creative mind; ability to create a compelling value story with payers and policymakers.
  • Team player with the ability to work collaboratively in a regional organization.
  • Executive presence; able to effectively represent the Company internally and externally.
  • Entrepreneurial, decisive, and have the tenacity to "make things happen."
  • A genuine care for patients and a desire to make a meaningful difference in their lives.


The level of this position will be based on the final candidate's qualifications.

Please note this job description is not designed to cover or contain a comprehensive listing of activities, duties or responsibilities that are required of the employee for this job. Duties, responsibilities and activities may change at any time with or without notice.

Novartis Gene Therapies is committed to creating a diverse environment and is proud to be an equal opportunity employer. All qualified applicants will receive consideration for employment without regard to race, color, religion, gender, gender identity, national origin, genetics, disability, age, sexual orientation or veteran status.