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Top Breaking News
The Ripple Effect of Alnylam (ALNY)'s Blow-up Yesterday     10/10/2016
Alnylam (ALNY) Stock Craters After Deaths Cause Clinical Trial to End     10/7/2016
Investors Sigh With Relief as bluebird bio (BLUE) Improves Its Gene Therapy Process     9/9/2016
23andMe Ancestry Tests Allegedly Have Issues With People of Color     8/30/2016
Spark Therapeutics (ONCE) Touts Long-Term Positive Phase III Gene Therapy Data     8/11/2016
Vtesse Bags Another $17 Million to Support Further Product Development and Expand Ongoing Clinical Trials     7/25/2016
First-Ever CRISPR Trial Points to Looming Problems     6/30/2016
Marinus Pharma (MRNS)'s Primary Endpoint Not Met in Ganaxolone Phase II     6/28/2016
Chiasma Chief Says Firm May Challenge FDA Over Rare-Disease Drug Rejection     5/12/2016
Astex Pharma (ASTX) and Genentech (RHHBY) Forge a Clinical Trial Deal for Acute Myeloid Leukemia     4/20/2016
FDA Slaps Clinical Hold on Ionis Pharma (IONS) Study While GlaxoSmithKline (GSK) Finalizes Protocol     4/7/2016
Alnylam (ALNY)’s John Maraganore Provides Leadership for RNAi Development and Biotech Industry     4/4/2016
Investors are Irked as BioMarin (BMRN)'s Pegvaliase Shows Mixed Results in Pivotal Study     3/21/2016
Positive Early Stage Pompe Data Allows Sanofi Genzyme (SNY) to Begin Phase III Trial this Summer     3/4/2016
Investors Sigh with Relief as BioMarin (BMRN)'s Batten Drug Meets Goal in Key Study     3/4/2016

News from Around the Web
Feeling Heavy, Light, Or About Right? Your Genes May Be To Blame, University of Colorado Study     9/1/2016
Should You Get Paid For Your DNA?     3/14/2016
Genetic Testing Company Opens Up Trove Of Cancer Patient Data To Public, Ambry Genetics Reveals     3/10/2016
The Environmental Influence On Epigenetics, National Institute of Environmental Health Sciences Study     7/24/2015
These Superhumans Are Real and Their DNA Could Be Worth Billions     7/22/2015
Project Pinpoints 12 New Genetic Causes Of Developmental Disorders, Wellcome Trust Sanger Institute Study     12/29/2014
Three-Parent Babies May Be Ready In Two Years, Human Fertilization and Embryology Authority Reveals     6/4/2014
Genetic Defect Predicts Cardiac Risk, University of Rochester Study     5/12/2011
Early Work Indicates Drug Used to Treat Alcoholism May Help Those With Fragile X and Autism, Indiana University School of Medicine Study     4/5/2011
Specific Genetic Mutations Associated with Preeclampsia, Hospital for Special Surgery Study     3/23/2011
Mouse Study Suggests New Clues to Celiac Disease, University of Chicago Study     2/10/2011
Blood-Clotting Agent Can Diagnose Fatal Genetic Diseases, University of Manchester Study Finds     2/4/2011
Study Shows Promise for New Drug to Treat Fragile X, Rush University Medical Center Study     1/10/2011
Decoding Fetal DNA From Mother's Blood Opens Door, Study Published in Science Translational Medicine     12/9/2010
Possible New Drug Targets for the Genetic Disorder Noonan Syndrome, Harvard Medical School Study     11/2/2010

Press Releases
Pairnomix Presents Systematic Approach To Identifying Approved Drugs That May Be Repurposed For Treatment Of Rare Genetic Diseases     12/5/2016
The Lancet Respiratory Medicine Publishes RAPID Extension Study Data On Effect Of Zemaira [Alpha1-Proteinase Inhibitor (Human)] In Patients With Alpha-1 Antitrypsin Deficiency (AATD)     12/2/2016
Deciphera Reports Encouraging Clinical Results With DCC-2618 In Genetically-Defined Cancers With Drug Resistant Mutations     12/1/2016
Agilis Biotherapeutics Announces Orphan Designation Approval In Europe For The Treatment Of AADC Deficiency     12/1/2016
Illumina (ILMN) Launches iHope Program To Identify Causes Of Undiagnosed Genetic Diseases In Children     12/1/2016
Vtesse Receives Rare Pediatric Disease Designation By The FDA For VTS-270 For The Treatment Of Niemann-Pick Type C1 Disease     11/29/2016
Apellis Pharma To Present Safety And Efficacy Data From Clinical Trials Of APL-2 In PNH At December Scientific Meetings     11/21/2016
Bay Area's Ultragenyx (RARE) Shelves Plan for a Quick Approval for Rare Disease Drug in Europe     11/11/2016
Sanofi Genzyme (SNY) Begins Pivotal Phase III Trial Of Neogaa Investigational Second-Generation Therapy For Pompe Disease     11/4/2016
La Jolla Pharma (LJPC) Receives Positive Opinion From European Orphan Committee For LJPC-401     10/24/2016
AGTC (AGTC) Files Investigational New Drug Application For The Treatment Of Achromatopsia Caused By Mutations In The CNGA3 Gene     10/20/2016
FDNA Launches New Face2Gene Suite Of Phenotyping Apps To Aid In Identification And Evaluation Of Rare And Ultra-Rare Genetic Disorders     10/18/2016
FDA, Clinuvel To Discuss SCENESSE At Pre-NDA Meeting     10/13/2016
Good Start Genetics Announces New Tier Of Offerings Making Genetic Testing More Accessible For Couples Planning A Family     10/13/2016
Alexion (ALXN) Release: New Long-Term Data Presented At WCPGHAN 2016 Show Rapid And Sustained Improvements In Important Markers Of Liver Injury And Lipid Abnormalities In Children And Adults With Lysosomal Acid Lipase Deficiency (LAL-D) Treated With Kanuma (Sebelipase Alfa)     10/7/2016