News | News By Subject | News by Disease News By Date | Search News

Genetic Disorder (misc) News Articles

Get Our FREE
Industry eNewsletter
Top Breaking News
Cambridge Biotech Agios (AGIO) Terminates AG-519 for PK Deficiency, But Continues AG-348 For Same Condition     12/19/2016
The Ripple Effect of Alnylam (ALNY)'s Blow-up Yesterday     10/10/2016
Alnylam (ALNY) Stock Craters After Deaths Cause Clinical Trial to End     10/7/2016
Investors Sigh With Relief as bluebird bio (BLUE) Improves Its Gene Therapy Process     9/9/2016
23andMe Ancestry Tests Allegedly Have Issues With People of Color     8/30/2016
Spark Therapeutics (ONCE) Touts Long-Term Positive Phase III Gene Therapy Data     8/11/2016
Vtesse Bags Another $17 Million to Support Further Product Development and Expand Ongoing Clinical Trials     7/25/2016
First-Ever CRISPR Trial Points to Looming Problems     6/30/2016
Marinus Pharma (MRNS)'s Primary Endpoint Not Met in Ganaxolone Phase II     6/28/2016
Chiasma Chief Says Firm May Challenge FDA Over Rare-Disease Drug Rejection     5/12/2016
Astex Pharma (ASTX) and Genentech (RHHBY) Forge a Clinical Trial Deal for Acute Myeloid Leukemia     4/20/2016
FDA Slaps Clinical Hold on Ionis Pharma (IONS) Study While GlaxoSmithKline (GSK) Finalizes Protocol     4/7/2016
Alnylam (ALNY)’s John Maraganore Provides Leadership for RNAi Development and Biotech Industry     4/4/2016
Investors are Irked as BioMarin (BMRN)'s Pegvaliase Shows Mixed Results in Pivotal Study     3/21/2016
Positive Early Stage Pompe Data Allows Sanofi Genzyme (SNY) to Begin Phase III Trial this Summer     3/4/2016

News from Around the Web
Bangladeshi Girl May Be First Female With 'Tree Man Syndrome'     2/2/2017
Feeling Heavy, Light, Or About Right? Your Genes May Be To Blame, University of Colorado Study     9/1/2016
Should You Get Paid For Your DNA?     3/14/2016
Genetic Testing Company Opens Up Trove Of Cancer Patient Data To Public, Ambry Genetics Reveals     3/10/2016
The Environmental Influence On Epigenetics, National Institute of Environmental Health Sciences Study     7/24/2015
These Superhumans Are Real and Their DNA Could Be Worth Billions     7/22/2015
Project Pinpoints 12 New Genetic Causes Of Developmental Disorders, Wellcome Trust Sanger Institute Study     12/29/2014
Three-Parent Babies May Be Ready In Two Years, Human Fertilization and Embryology Authority Reveals     6/4/2014
Genetic Defect Predicts Cardiac Risk, University of Rochester Study     5/12/2011
Early Work Indicates Drug Used to Treat Alcoholism May Help Those With Fragile X and Autism, Indiana University School of Medicine Study     4/5/2011
Specific Genetic Mutations Associated with Preeclampsia, Hospital for Special Surgery Study     3/23/2011
Mouse Study Suggests New Clues to Celiac Disease, University of Chicago Study     2/10/2011
Blood-Clotting Agent Can Diagnose Fatal Genetic Diseases, University of Manchester Study Finds     2/4/2011
Study Shows Promise for New Drug to Treat Fragile X, Rush University Medical Center Study     1/10/2011
Decoding Fetal DNA From Mother's Blood Opens Door, Study Published in Science Translational Medicine     12/9/2010

Press Releases
Horizon Pharma (HZNP) To Present Data On RAVICTI (Glycerol Phenylbutyrate) Oral Liquid For Urea Cycle Disorder Patients Aged Two Months To Two Years     3/22/2017
Abeona Therapeutics Receives Orphan Drug Designation In The European Union For EB-101 Gene Therapy Clinical Trial For Epidermolysis Bullosa     3/8/2017
90% Of The Cases Analysed Are Carriers Of At Least One Genetic Mutation: iGenomX     3/2/2017
Attune Announces Late-Breaking Poster Presentation Of ATN-249, An Oral Kallikrein Inhibitor For The Treatment Of HAE     3/1/2017
Fibrocell (FCSC) Announces Dosing Of First Patient In Phase I/II Clinical Trial Of FCX-007 Gene Therapy For Treatment Of Recessive Dystrophic Epidermolysis Bullosa     2/23/2017
Abeona Therapeutics Provides Update From ABO-102 Phase I/II MPS IIIA Clinical Trial At The 13th Annual WORLDSymposium 2017     2/17/2017
Invitae Release: New Research Suggests Broader Genetic Testing Of Prostate Cancer Patients May Be Warranted To Identify Risk Of An Inherited Mutation That Might Inform Treatment     2/17/2017
Zogenix (ZGNX) Announces Initiation Of Clinical Efficacy Portion Of Study 1504 For ZX008 In Dravet Syndrome     2/13/2017
Viking Therapeutics (VKTX) Announces Initial Results From In Vivo Proof-Of-Concept Study Of VK2809 In Glycogen Storage Disease Ia (GSD Ia)     2/9/2017
Experimental Biology and Medicine Release: miRNA Modulators Of Transcription Factor Targets: Potential Treatments For Hemoglobinopathies     2/9/2017
MeiraGTx Provides Clinical Trial Updates For Achromatopsia And Leber's Congenital Amaurosis Ocular Gene Therapy Programs     2/8/2017
Reproductive Genetics To Enable Higher Success Rates And Prevent Transmission Of Genetic Disorders: iGenomX     2/7/2017
Sobi Obtains Approval From The European Commission (EC) For New Dosing Frequency Of Orfadin     2/2/2017
X4 Pharma Announces Initiation Of A Phase 2/3 Clinical Study Of X4P-001-LD In Patients With WHIM Syndrome, A Rare Genetic Primary Immunodeficiency Disease     1/30/2017
Genepeeks Release: Company Launches Preconception Test For Combined Risk Of Passing On More Than 1,000 Serious Genetic Diseases     1/24/2017