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Top Breaking News
Shire (SHPG)'s $6.5 Billion Dyax (DYAX) Bet Pays Off as Lanadelumab Wows in Phase III Study     5/18/2017
Safety Concerns Raised as Ionis Pharma (IONS)'s Inotersen Meets Both Primary Endpoints in Late-Stage Study     5/16/2017
Wowsers! FDA Approves BioMarin (BMRN)'s Brineura, the First Drug for Batten Disease     5/2/2017
FDA Calls Regeneron (REGN)'s Evinacumab a Breakthrough     4/7/2017
Cambridge Biotech Agios (AGIO) Terminates AG-519 for PK Deficiency, But Continues AG-348 For Same Condition     12/19/2016
The Ripple Effect of Alnylam (ALNY)'s Blow-up Yesterday     10/10/2016
Alnylam (ALNY) Stock Craters After Deaths Cause Clinical Trial to End     10/7/2016
Investors Sigh With Relief as bluebird bio (BLUE) Improves Its Gene Therapy Process     9/9/2016
23andMe Ancestry Tests Allegedly Have Issues With People of Color     8/30/2016
Spark Therapeutics (ONCE) Touts Long-Term Positive Phase III Gene Therapy Data     8/11/2016
Vtesse Bags Another $17 Million to Support Further Product Development and Expand Ongoing Clinical Trials     7/25/2016
First-Ever CRISPR Trial Points to Looming Problems     6/30/2016
Marinus Pharma (MRNS)'s Primary Endpoint Not Met in Ganaxolone Phase II     6/28/2016
Chiasma Chief Says Firm May Challenge FDA Over Rare-Disease Drug Rejection     5/12/2016
Astex Pharma (ASTX) and Genentech (RHHBY) Forge a Clinical Trial Deal for Acute Myeloid Leukemia     4/20/2016

News from Around the Web
CRISPR Cousin SHERLOCK May Be Able To Track Down Diseases, Broad Institute Scientists Say     4/14/2017
Alnylam (ALNY)'s Patisiran, Chronicle Of A Death Foretold     4/11/2017
This DNA-Testing Company Is Offering Patients A Chance To Help Find A Cure For Their Conditions     4/7/2017
Bangladeshi Girl May Be First Female With 'Tree Man Syndrome'     2/2/2017
Feeling Heavy, Light, Or About Right? Your Genes May Be To Blame, University of Colorado Study     9/1/2016
Should You Get Paid For Your DNA?     3/14/2016
Genetic Testing Company Opens Up Trove Of Cancer Patient Data To Public, Ambry Genetics Reveals     3/10/2016
The Environmental Influence On Epigenetics, National Institute of Environmental Health Sciences Study     7/24/2015
These Superhumans Are Real and Their DNA Could Be Worth Billions     7/22/2015
Project Pinpoints 12 New Genetic Causes Of Developmental Disorders, Wellcome Trust Sanger Institute Study     12/29/2014
Three-Parent Babies May Be Ready In Two Years, Human Fertilization and Embryology Authority Reveals     6/4/2014
Genetic Defect Predicts Cardiac Risk, University of Rochester Study     5/12/2011
Early Work Indicates Drug Used to Treat Alcoholism May Help Those With Fragile X and Autism, Indiana University School of Medicine Study     4/5/2011
Specific Genetic Mutations Associated with Preeclampsia, Hospital for Special Surgery Study     3/23/2011
Mouse Study Suggests New Clues to Celiac Disease, University of Chicago Study     2/10/2011

Press Releases
Abeona Therapeutics Receives FDA Orphan Drug Designation For EB-101 Gene Therapy Product For Patients With Epidermolysis Bullosa     5/25/2017
Kamada Ltd. (KMDA) Presents Updated Data From Phase II Clinical Trial Of Inhaled Alpha-1-Antitrypsin For Treatment Of Alpha-1 Antitrypsin Deficiency At 2017 American Thoracic Society International Conference     5/24/2017
Berg Announces New Partnership With Debra Of America To Tackle Epidermolysis Bullosa-A Rare Genetic Tissue Disorder     5/15/2017
Abeona Therapeutics Announces Top-Line Data For ABO-102 Phase I/II MPS IIIA Gene Therapy Trial At ASGCT     5/12/2017
Loxo Oncology (LOXO) Announces FDA Orphan Drug Designation Granted To Larotrectinib For The Treatment Of Solid Tumors With NTRK-Fusion Proteins     5/12/2017
AGTC (AGTC) Presents New Data On Its AAV-Based Gene Therapies For The Treatment Of Achromatopsia And X-Linked Retinitis Pigmentosa At The American Society Of Gene And Cell Therapy 20th Annual Meeting     5/11/2017
Orphazyme Completes Enrollment Of Patients For Phase III Clinical Trial In Niemann-Pick Type C Disease     5/11/2017
Seattle Children's Hospital Release: Research Links Genetics To Early-Onset Pancreatitis In Pediatric Patients     5/11/2017
iGenomX's Carrier Genetic Test Can Save Children From Inheriting Genetic Disorders     5/8/2017
Rhythm Starts Phase III Clinical Trial Of Setmelanotide For Rare Genetic Disorder Of Obesity     5/4/2017
Cincinnati Children's Hospital Medical Center Release: Study Suggests Genetic Reason for Impaired Skilled Movements     5/4/2017
Abeona Therapeutics Provides Update On EB-101 Gene Therapy For Severe Form Of Epidermolysis Bullosa From The Society For Investigative Dermatology Conference     5/2/2017
Sanofi Genzyme (SNY) Announces Approval Of Cerdelga (Eliglustat Capsules) By Health Canada For Rare Genetic Condition     5/1/2017
ProQR Therapeutics B.V. (PRQR) Announces Clearance Of IND Application To Start Clinical Trial For QR-110 In Leber’s Congenital Amaurosis Type 10 Patients     4/27/2017
PhaseRx (PZRX) Receives Positive Opinion For Orphan Drug Designation For PRX-OTC From EMA     4/25/2017

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