PTC Therapeutics's New $35,000 Price Tag For MD Drug Draws Criticism And Doubt

Christine McSherry is used to a fight. Her son, Jett, was diagnosed with Duchenne muscular dystrophy, a rare, debilitating condition, when he was 5. He lost the ability to walk just before he turned 14.

McSherry has become an outspoken advocate for Jett and other kids with Duchenne, particularly in fighting for access to drugs she's convinced help against the disease's devastating effects.

What she didn't expect to be fighting for was access to a medicine Jett was already using.

Back to news