Dompe Announces the FDA Has Granted Orphan Drug Designation to Its rhNGF-Based Treatment for Retinitis Pigmentosa

MILAN--(BUSINESS WIRE)--Dompé, the leading company in research & development of novel treatment solutions for rare diseases, announces its investigational drug based on the recombinant human nerve growth factor (rhNGF) discovered by Nobel Laureate Professor Rita Levi Montalcini has been granted orphan drug designation by the US FDA for the treatment of retinitis pigmentosa (RP). This gives new hope for the treatment of this disease for which at present there is no cure. The orphan drug designation by the FDA comes just a few months after orphan drug designation was granted by the European Medicine Agency (EMA) and marks another milestone for this investigational drug, which is already in late-stage clinical development for the treatment of neurotrophic keratitis, a severe corneal disease.

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